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Dominant-negative kinase domain mutations in FGFR1 can explain the clinical severity of Hartsfield syndrome

Mutations in FGFR1 have recently been associated with Hartsfield syndrome, a clinically distinct syndromic form of holoprosencephaly (HPE) with ectrodactly, which frequently includes combinations of craniofacial, limb and brain abnormalities not typical for classical HPE. Unrelated clinical conditio...

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Dettagli Bibliografici
Pubblicato in:Hum Mol Genet
Autori principali: Hong, Sungkook, Hu, Ping, Marino, Juliana, Hufnagel, Sophia B., Hopkin, Robert J., Toromanović, Alma, Richieri-Costa, Antonio, Ribeiro-Bicudo, Lucilene A., Kruszka, Paul, Roessler, Erich, Muenke, Maximilian
Natura: Artigo
Lingua:Inglês
Pubblicazione: Oxford University Press 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5062582/
https://ncbi.nlm.nih.gov/pubmed/26931467
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddw064
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