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Efficacy and safety of i.v. sodium benzoate in urea cycle disorders: a multicentre retrospective study

BACKGROUND: The efficacy and safety of intra-venous (i.v.) sodium benzoate for treating acute episodes of hyperammonemia in urea cycle enzyme disorders (UCD) is well known. However, published data do not provide a clear picture of the benefits and risks of this drug. We report a retrospective multic...

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Pubblicato in:Orphanet J Rare Dis
Autori principali: Husson, Marie-Caroline, Schiff, Manuel, Fouilhoux, Alain, Cano, Aline, Dobbelaere, Dries, Brassier, Anais, Mention, Karine, Arnoux, Jean-Baptiste, Feillet, François, Chabrol, Brigitte, Guffon, Nathalie, Elie, Caroline, de Lonlay, Pascale
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5034629/
https://ncbi.nlm.nih.gov/pubmed/27663197
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-016-0513-0
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