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Advances in gene therapy for muscular dystrophies

Duchenne muscular dystrophy (DMD) is a recessive lethal inherited muscular dystrophy caused by mutations in the gene encoding dystrophin, a protein required for muscle fibre integrity. So far, many approaches have been tested from the traditional gene addition to newer advanced approaches based on m...

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Detalhes bibliográficos
Publicado no:F1000Res
Main Authors: Abdul-Razak, Hayder, Malerba, Alberto, Dickson, George
Formato: Artigo
Idioma:Inglês
Publicado em: F1000Research 2016
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4991540/
https://ncbi.nlm.nih.gov/pubmed/27594988
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.12688/f1000research.8735.1
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