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Advances of gene therapy for primary immunodeficiencies

In the recent past, the gene therapy field has witnessed a remarkable series of successes, many of which have involved primary immunodeficiency diseases, such as X-linked severe combined immunodeficiency, adenosine deaminase deficiency, chronic granulomatous disease, and Wiskott-Aldrich syndrome. Wh...

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Detalhes bibliográficos
Publicado no:F1000Res
Autor principal: Candotti, Fabio
Formato: Artigo
Idioma:Inglês
Publicado em: F1000Research 2016
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4963077/
https://ncbi.nlm.nih.gov/pubmed/27508076
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.12688/f1000research.7512.1
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