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Pulmonary alveolar proteinosis and Niemann Pick disease type B: An unexpected combination

BACKGROUND: Pulmonary involvement in Niemann-Pick disease (NPD) is a common finding, especially in type B. It usually manifests with symptoms of restrictive lung disease appearing in adulthood but showing gradual deterioration over time. Treatment options have been dramatically limited, with whole l...

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Dettagli Bibliografici
Pubblicato in:Respir Med Case Rep
Autori principali: Sideris, Georgios Antonios, Josephson, Maureen
Natura: Artigo
Lingua:Inglês
Pubblicazione: Elsevier 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4932622/
https://ncbi.nlm.nih.gov/pubmed/27408787
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.rmcr.2016.06.009
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