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Current and future treatment options for cystic fibrosis lung disease: latest evidence and clinical implications

Treatment for cystic fibrosis (CF) has conventionally targeted downstream consequences of the defect such as mucus plugging and infection. More recently, significant advances have been made in treating the root cause of the disease, namely a defective CF transmembrane conductance regulator (CFTR) ge...

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Dettagli Bibliografici
Pubblicato in:Ther Adv Chronic Dis
Autori principali: Edmondson, Claire, Davies, Jane C.
Natura: Artigo
Lingua:Inglês
Pubblicazione: SAGE Publications 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4907071/
https://ncbi.nlm.nih.gov/pubmed/27347364
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1177/2040622316641352
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