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Favorable Growth Hormone Treatment Response in a Young Boy with Achondroplasia

BACKGROUND: Achondroplasia is a skeletal dysplasia, the most common cause of rhizomelic dwarfism. CASE PRESENTATION: This is a ten year old boy who was first diagnosed prenatally. He had a mutation c1138G>A in the gene FGFR3 in a heterozygotic constellation. His IGF1 and IGFBP3 levels were normal...

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Опубликовано в: :Med Arch
Главные авторы: Krstevska-Konstantinova, Marina, Stamatova, Ana, Gucev, Zoran
Формат: Artigo
Язык:Inglês
Опубликовано: AVICENA, d.o.o., Sarajevo 2016
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Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC4851542/
https://ncbi.nlm.nih.gov/pubmed/27147792
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.5455/medarh.2016.70.148-150
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