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Selective Neuromuscular Denervation in Taiwanese Severe SMA Mouse Can Be Reversed by Morpholino Antisense Oligonucleotides

Spinal muscular atrophy (SMA) is an autosomal recessive motor neuron disease caused by deficiency of the survival of motor neuron (SMN) protein, which leads to synaptic defects and spinal motor neuron death. Neuromuscular junction (NMJ) abnormalities have been found to be involved in SMA pathogenesi...

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Dettagli Bibliografici
Pubblicato in:PLoS One
Autori principali: Lin, Te-Lin, Chen, Tai-Heng, Hsu, Ya-Yun, Cheng, Yu-Hua, Juang, Bi-Tzen, Jong, Yuh-Jyh
Natura: Artigo
Lingua:Inglês
Pubblicazione: Public Library of Science 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4849667/
https://ncbi.nlm.nih.gov/pubmed/27124114
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1371/journal.pone.0154723
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