A carregar...

Neutralizing Antibodies Against Adeno-Associated Viral Capsids in Patients with mut Methylmalonic Acidemia

Isolated methylmalonic acidemia (MMA), a group of autosomal recessive inborn errors of metabolism, is most commonly caused by complete (mut(0)) or partial (mut(−)) deficiency of the enzyme methylmalonyl-CoA mutase (MUT). The severe metabolic instability and increased mortality experienced by many af...

ver descrição completa

Na minha lista:
Detalhes bibliográficos
Publicado no:Hum Gene Ther
Main Authors: Harrington, Elizabeth A., Sloan, Jennifer L., Manoli, Irini, Chandler, Randy J., Schneider, Mark, McGuire, Peter J., Calcedo, Roberto, Wilson, James M., Venditti, Charles P.
Formato: Artigo
Idioma:Inglês
Publicado em: Mary Ann Liebert, Inc. 2016
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4841085/
https://ncbi.nlm.nih.gov/pubmed/26790480
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2015.092
Tags: Adicionar Tag
Sem tags, seja o primeiro a adicionar uma tag!