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Endocrine Dysfunction in Diamond Blackfan Anemia (DBA): A Report from the DBA Registry (DBAR)

OBJECTIVE: Diamond Blackfan anemia (DBA) is a rare inherited bone marrow failure syndrome. The mainstays of treatment involve chronic red cell transfusions, long-term glucocorticoid therapy, and stem cell transplantation. Systematic data concerning endocrine function in DBA are limited. We studied p...

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Dettagli Bibliografici
Pubblicato in:Pediatr Blood Cancer
Autori principali: Lahoti, Amit, Harris, Yael T, Speiser, Phyllis W, Atsidaftos, Evangelia, Lipton, Jeffrey M, Vlachos, Adrianna
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2015
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4829065/
https://ncbi.nlm.nih.gov/pubmed/26496000
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/pbc.25780
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