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CHCHD10 variant p.(Gly66Val) causes axonal Charcot-Marie-Tooth disease

OBJECTIVE: We describe the phenotype consistent with axonal Charcot-Marie-Tooth disease type 2 (CMT2) in 4 families with a c.197G>T (p.(Gly66Val)) variant in CHCHD10. METHODS: We sequenced the CHCHD10 gene in a cohort of 107 families with CMT2 of unknown etiology. The patients were characterized...

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Publicat a:Neurol Genet
Autors principals: Auranen, Mari, Ylikallio, Emil, Shcherbii, Maria, Paetau, Anders, Kiuru-Enari, Sari, Toppila, Jussi P., Tyynismaa, Henna
Format: Artigo
Idioma:Inglês
Publicat: Wolters Kluwer 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4821082/
https://ncbi.nlm.nih.gov/pubmed/27066538
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/NXG.0000000000000003
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