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Robust Long-term Transduction of Common Marmoset Neuromuscular Tissue With rAAV1 and rAAV9

Profiles of recombinant adeno-associated virus (rAAV)-mediated transduction show interspecies differences for each AAV serotype. Robust long-term transgene expression is generally observed in rodents, whereas insufficient transduction is seen in animals with more advanced immune systems. Non-human p...

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Библиографические подробности
Опубликовано в: :Mol Ther Nucleic Acids
Главные авторы: Okada, Hironori, Ishibashi, Hidetoshi, Hayashita-Kinoh, Hiromi, Chiyo, Tomoko, Nitahara-Kasahara, Yuko, Baba, Yukihiro, Watanabe, Sumiko, Takeda, Shin'ichi, Okada, Takashi
Формат: Artigo
Язык:Inglês
Опубликовано: Nature Publishing Group 2013
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC4817936/
https://ncbi.nlm.nih.gov/pubmed/23715217
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mtna.2013.21
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