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Let There Be Light: Gene and Cell Therapy for Blindness

Retinal degenerative diseases are a leading cause of irreversible blindness. Retinal cell death is the main cause of vision loss in genetic disorders such as retinitis pigmentosa, Stargardt disease, and Leber congenital amaurosis, as well as in complex age-related diseases such as age-related macula...

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Dades bibliogràfiques
Publicat a:Hum Gene Ther
Autors principals: Dalkara, Deniz, Goureau, Olivier, Marazova, Katia, Sahel, José-Alain
Format: Artigo
Idioma:Inglês
Publicat: Mary Ann Liebert, Inc. 2016
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4779297/
https://ncbi.nlm.nih.gov/pubmed/26751519
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2015.147
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