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mRNA and microRNA transcriptomics analyses in a murine model of dystrophin loss and therapeutic restoration

Duchenne muscular dystrophy (DMD) is a pediatric, X-linked, progressive muscle-wasting disorder caused by loss of function mutations affecting the gene encoding the dystrophin protein. While the primary genetic insult in DMD is well described, many details of the molecular and cellular pathologies t...

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Dades bibliogràfiques
Publicat a:Genom Data
Autors principals: Roberts, Thomas C., Blomberg, K. Emelie M., Smith, C.I. Edvard, EL Andaloussi, Samir, Wood, Matthew J.A.
Format: Artigo
Idioma:Inglês
Publicat: Elsevier 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4778658/
https://ncbi.nlm.nih.gov/pubmed/26981371
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.gdata.2015.11.025
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