Загрузка...
Gene therapy for Wiskott-Aldrich Syndrome—Long-term reconstitution and clinical benefits, but increased risk for leukemogenesis
Wiskott-Aldrich-Syndrome (WAS) is a rare X-linked recessive disease caused by mutations of the WAS gene. It is characterized by immunodeficiency, autoimmunity, low numbers of small platelets (microthrombocytopenia) and a high risk of cancer, especially B cell lymphoma and leukemia.
Сохранить в:
| Опубликовано в: : | Rare Dis |
|---|---|
| Главные авторы: | , , , , , , |
| Формат: | Artigo |
| Язык: | Inglês |
| Опубликовано: |
Taylor & Francis
2014
|
| Предметы: | |
| Online-ссылка: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4755244/ https://ncbi.nlm.nih.gov/pubmed/26942098 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4161/21675511.2014.947749 |
| Метки: |
Добавить метку
Нет меток, Требуется 1-ая метка записи!
|