Long-term effectiveness of agalsidase alfa enzyme replacement in Fabry disease: A Fabry Outcome Survey analysis

Outcomes from 5 years of treatment with agalsidase alfa enzyme replacement therapy (ERT) for Fabry disease in patients enrolled in the Fabry Outcome Survey (FOS) were compared with published findings for untreated patients with Fabry disease. Data were extracted from FOS, a Shire-sponsored database,...

Descrizione completa

Salvato in:
Dettagli Bibliografici
Pubblicato in:Mol Genet Metab Rep
Autori principali: Beck, Michael, Hughes, Derralynn, Kampmann, Christoph, Larroque, Sylvain, Mehta, Atul, Pintos-Morell, Guillem, Ramaswami, Uma, West, Michael, Wijatyk, Anna, Giugliani, Roberto
Natura: Artigo
Lingua:Inglês
Pubblicazione: Elsevier 2015
Soggetti:
SI:Therapy
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4750577/
https://ncbi.nlm.nih.gov/pubmed/26937390
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgmr.2015.02.002
Tags: Aggiungi Tag
Nessun Tag, puoi essere il primo ad aggiungerne! !

Documenti analoghi