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A National Approach to Reimbursement Decision-Making on Drugs for Rare Diseases in Canada? Insights from Across the Ponds

INTRODUCTION: Regardless of the type of health system or payer, coverage decisions on drugs for rare diseases (DRDs) are challenging. While these drugs typically represent the only active treatment option for a progressive and/or life-threatening condition, evidence of clinical benefit is often limi...

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Detalles Bibliográficos
Publicado en:Healthc Policy
Autores principales: Short, Hilary, Stafinski, Tania, Menon, Devidas
Formato: Artigo
Lenguaje:Inglês
Publicado: Longwoods Publishing 2015
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC4748348/
https://ncbi.nlm.nih.gov/pubmed/26142357
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