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A Novel Splice Site Mutation in SMARCAL1 Results in Aberrant Exon Definition in a Child with Schimke Immunoosseous Dysplasia

Schimke Immunoosseous Dysplasia (SIOD) is a rare, autosomal recessive disorder of childhood characterized by spondyloepiphyseal dysplasia, focal segmental glomerulosclerosis and renal failure, T-cell immunodeficiency, and cancer in certain instances. Approximately half of patients with SIOD are repo...

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Detalhes bibliográficos
Publicado no:Am J Med Genet A
Main Authors: Carroll, Clinton, Hunley, Tracy E., Guo, Yan, Cortez, David
Formato: Artigo
Idioma:Inglês
Publicado em: 2015
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4743909/
https://ncbi.nlm.nih.gov/pubmed/25943327
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ajmg.a.37146
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