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Histologic muscular history in steroid-treated and untreated patients with Duchenne dystrophy

OBJECTIVE: Duchenne muscular dystrophy (DMD) is a lethal disease. The outcome measures used in numerous therapeutic trials include skeletal muscle biopsy. We studied the natural history of DMD from the standpoint of muscle histology with the aim of providing a reproducible tool for use in evaluating...

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Dettagli Bibliografici
Pubblicato in:Neurology
Autori principali: Peverelli, Lorenzo, Testolin, Silvia, Villa, Luisa, D'Amico, Adele, Petrini, Stefania, Favero, Chiara, Magri, Francesca, Morandi, Lucia, Mora, Marina, Mongini, Tiziana, Bertini, Enrico, Sciacco, Monica, Comi, Giacomo P., Moggio, Maurizio
Natura: Artigo
Lingua:Inglês
Pubblicazione: Lippincott Williams & Wilkins 2015
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4662699/
https://ncbi.nlm.nih.gov/pubmed/26497992
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/WNL.0000000000002147
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