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Gene replacement rescues severe muscle pathology and prolongs survival in myotubularin-deficient mice and dogs

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Foilsithe in:Ann Transl Med
Main Authors: Childers, Martin K., Beggs, Alan H., Buj-Bello, Ana
Formáid: Artigo
Teanga:Inglês
Foilsithe: AME Publishing Company 2015
Ábhair:
Rochtain Ar Líne:https://ncbi.nlm.nih.gov/pmc/articles/PMC4620094/
https://ncbi.nlm.nih.gov/pubmed/26605303
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3978/j.issn.2305-5839.2015.10.01
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