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Cost-effectiveness analysis and prevention effects of ultra-orphan drugs for rare diseases: an in silico model applied to Cryopyrin Associated Periodic Syndromes (CAPS)

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Bibliografske podrobnosti
izdano v:Pediatr Rheumatol Online J
Main Authors: Trieste, L, Della Casa Alberighi, O, Turchetti, G, Pierotti, F, Accame, L, Lorenzoni, V, Frenkel, J, Gattorno, M, Quartier, P, Martini, A
Format: Artigo
Jezik:Inglês
Izdano: BioMed Central 2015
Teme:
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC4599848/
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/1546-0096-13-S1-P185
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