Effectiveness of agalsidase alfa enzyme replacement in Fabry disease: cardiac outcomes after 10 years’ treatment

BACKGROUND: To explore long-term effects of agalsidase alfa on Fabry disease cardiomyopathy in adults. METHODS: Retrospective analysis of prospectively collected data at a single center in Mainz, Germany, revealed that 45 adult patients (21 men, 24 women) had received agalsidase alfa for approximate...

Full description

Saved in:
Bibliographic Details
Published in:Orphanet J Rare Dis
Main Authors: Kampmann, Christoph, Perrin, Amandine, Beck, Michael
Format: Artigo
Language:Inglês
Published: BioMed Central 2015
Subjects:
Research
Online Access:https://ncbi.nlm.nih.gov/pmc/articles/PMC4587871/
https://ncbi.nlm.nih.gov/pubmed/26416388
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-015-0338-2
Tags: Add Tag
No Tags, Be the first to tag this record!

Similar Items