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Efficacy and Safety of a Microsomal Triglyceride Transfer Protein Inhibitor in Homozygous Familial Hypercholesterolemia

BACKGROUND: Patients with homozygous familial hypercholesterolemia (HoFH) respond inadequately to existing drugs. We conducted a phase 3 study to assess the efficacy and safety of the microsomal triglyceride transfer protein inhibitor lomitapide in adults with HoFH. METHODS: Twenty-nine subjects enr...

Täydet tiedot

Tallennettuna:
Bibliografiset tiedot
Julkaisussa:Lancet
Päätekijät: Cuchel, M, Meagher, EA, du Toit, Theron H., Blom, DJ, Marais, AD, Hegele, RA, Averna, M, Sirtori, C, Shah, PK, Gaudet, D, Stefanutti, C, Vigna, GB, Du Plessis, AME, Propert, Kathleen J., Sasiela, WJ, Bloedon, LT, Rader, DJ
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: 2012
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC4587657/
https://ncbi.nlm.nih.gov/pubmed/23122768
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/S0140-6736(12)61731-0
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