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Clinical Findings and Natural History in Ten Unrelated Families with Juvenile and Adult GM1 Gangliosidosis

We describe 12 subjects of ten unrelated families from the region of Campinas and the southern state of Minas Gerais, Brazil, who presented with juvenile (n = 4) and adult (n = 8) GM1 gangliosidosis. Data includes clinical history, physical examination, and ancillary exam findings. Six subjects pres...

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Detalhes bibliográficos
Publicado no:JIMD Rep
Main Authors: Kannebley, João Stein, Silveira-Moriyama, Laura, Bastos, Laís Orrico Donnabella, Steiner, Carlos Eduardo
Formato: Artigo
Idioma:Inglês
Publicado em: Springer Berlin Heidelberg 2015
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4582032/
https://ncbi.nlm.nih.gov/pubmed/26108645
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2015_451
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