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IGF-1 in Friedreich’s Ataxia – proof-of-concept trial
BACKGROUND: Friedreich’s ataxia is an autosomal recessive, severely incapacitating disorder. There is little objective evidence regarding FRDA management. Abnormalities in the insulin/insulin-like growth factor 1 (IGF-1) system (IIS) signalling pathway were thought to play a role in the physiopathol...
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| Publicat a: | Cerebellum Ataxias |
|---|---|
| Autors principals: | , , |
| Format: | Artigo |
| Idioma: | Inglês |
| Publicat: |
BioMed Central
2014
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| Matèries: | |
| Accés en línia: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4552279/ https://ncbi.nlm.nih.gov/pubmed/26331034 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/2053-8871-1-10 |
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