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Decision Analysis of Treatment Strategies in Children with Severe Sickle Cell Disease

We designed a decision analysis model comparing four treatment strategies for severe sickle cell disease: no intervention, hydroxyurea, chronic transfusion, or stem cell transplant. The treatment strategy associated with the highest average utility (quality of life) was stem cell transplant (0.85)....

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Dades bibliogràfiques
Publicat a:J Pediatr Hematol Oncol
Autors principals: O'Brien, Sarah H., Hankins, Jane S.
Format: Artigo
Idioma:Inglês
Publicat: 2009
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4486015/
https://ncbi.nlm.nih.gov/pubmed/19829150
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/MPH.0b013e3181b83cab
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