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Cost–Consequence Analysis of Nitisinone for Treatment of Tyrosinemia Type I

BACKGROUND: Tyrosinemia type I is a rare but severe genetic metabolic disorder. Nitisinone combined with a diet low in tyrosine and phenylalanine became first-line therapy in 1994. OBJECTIVES: To estimate the direct medical costs of health care services related to the treatment of tyrosinemia type I...

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Publicat a:Can J Hosp Pharm
Autors principals: Simoncelli, Mariève, Samson, Johanne, Bussières, Jean-François, Lacroix, Jacques, Dorais, Marc, Battista, Renaldo, Perreault, Sylvie
Format: Artigo
Idioma:Inglês
Publicat: Canadian Society of Hospital Pharmacists 2015
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4485508/
https://ncbi.nlm.nih.gov/pubmed/26157182
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