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Identification of the gene defect responsible for severe hypercholesterolaemia using whole-exome sequencing

Familial hypercholesterolaemia (FH) is a serious genetic metabolic disease. We identified a specific family in which the proband had typical homozygous phenotype of FH, but couldn’t detect any mutations in usual pathogenic genes using traditional sequencing. This study is the first attempt to use wh...

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Dettagli Bibliografici
Pubblicato in:Sci Rep
Autori principali: Sun, Li-Yuan, Zhang, Yong-Biao, Jiang, Long, Wan, Ning, Wu, Wen-Feng, Pan, Xiao-Dong, Yu, Jun, Zhang, Feng, Wang, Lu-Ya
Natura: Artigo
Lingua:Inglês
Pubblicazione: Nature Publishing Group 2015
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4468422/
https://ncbi.nlm.nih.gov/pubmed/26077743
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/srep11380
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