Impact of imiglucerase supply constraint on the therapeutic management and course of disease in French patients with Gaucher disease type 1

BACKGROUND: In 2009, a worldwide supply constraint of imiglucerase led to treatment modifications or interruptions for patients with Gaucher disease (GD) type 1. In France, joint treatment recommendations were issued to protect the most vulnerable patients. This observational study evaluated the imp...

Volledige beschrijving

Bewaard in:
Bibliografische gegevens
Gepubliceerd in:Orphanet J Rare Dis
Hoofdauteurs: Stirnemann, Jérôme, Rose, Christian, Serratrice, Christine, Dalbies, Florence, Lidove, Olivier, Masseau, Agathe, Pers, Yves-Marie, Baron, Camille, Belmatoug, Nadia
Formaat: Artigo
Taal:Inglês
Gepubliceerd in: BioMed Central 2015
Onderwerpen:
Research
Online toegang:https://ncbi.nlm.nih.gov/pmc/articles/PMC4434532/
https://ncbi.nlm.nih.gov/pubmed/25968608
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-015-0275-0
Tags: Voeg label toe
Geen labels, Wees de eerste die dit record labelt!

Gelijkaardige items