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Lessons from two cases: is Fabry disease the correct diagnosis?

Fabry disease (FD) is an X linked inherited lysosomal storage disorder with complex multisystem involvement; it is caused by deficiency of the lysosomal enzyme α-galactosidase. Deficient enzyme activity leads to a wide spectrum of clinical manifestations consisting of dermatological, ophthalmologica...

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Detalhes bibliográficos
Publicado no:BMJ Case Rep
Main Authors: Kiykim, Ertugrul, Aktuglu Zeybek, Cigdem Ayse, Zubarioglu, Tanyel, Aydin, Ahmet
Formato: Artigo
Idioma:Inglês
Publicado em: BMJ Publishing Group 2015
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4434327/
https://ncbi.nlm.nih.gov/pubmed/25969484
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/bcr-2014-208150
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