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Letter to the Editors: Concerning “CRIM-Negative Pompe Disease Patients with Satisfactory Clinical Outcomes on Enzyme Replacement Therapy” by Al Khallaf et al

Wedi'i Gadw mewn:
Manylion Llyfryddiaeth
Cyhoeddwyd yn:J Inherit Metab Dis
Prif Awduron: Prater, Sean N., Banugaria, Suhrad G., Morgan, Claire, Sung, Crystal C., Rosenberg, Amy S., Kishnani, Priya S.
Fformat: Artigo
Iaith:Inglês
Cyhoeddwyd: 2013
Pynciau:
Mynediad Ar-lein:https://ncbi.nlm.nih.gov/pmc/articles/PMC4353589/
https://ncbi.nlm.nih.gov/pubmed/23887636
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s10545-013-9637-8
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