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Molecular mechanisms in DM1 — a focus on foci

Myotonic dystrophy type 1 is caused by abnormal expansion of a CTG-trinucleotide repeat in the gene encoding Dystrophia Myotonica Protein Kinase (DMPK), which in turn leads to global deregulation of gene expression in affected individuals. The transcribed mRNA contains a massive CUG-expansion in the...

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Bibliografiske detaljer
Udgivet i:Nucleic Acids Res
Main Authors: Pettersson, Olof Joakim, Aagaard, Lars, Jensen, Thomas Gryesten, Damgaard, Christian Kroun
Format: Artigo
Sprog:Inglês
Udgivet: Oxford University Press 2015
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC4344492/
https://ncbi.nlm.nih.gov/pubmed/25605794
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/nar/gkv029
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