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Composite biomarkers for assessing Duchenne muscular dystrophy: an initial assessment

BACKGROUND: Compared to individual parameters, composite biomarkers may provide a more effective means for monitoring disease progression and the effects of therapy in clinical trials than single measures. In this study, we built composite biomarkers for use in Duchenne muscular dystrophy (DMD) by c...

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Detaylı Bibliyografya
Yayımlandı:Pediatr Neurol
Asıl Yazarlar: Shklyar, Irina, Pasternak, Amy, Kapur, Kush, Darras, Basil T., Rutkove, Seward B.
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: 2014
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC4336219/
https://ncbi.nlm.nih.gov/pubmed/25447928
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.pediatrneurol.2014.09.014
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