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Expanding the Phenotypic Spectrum and Variability of Endocrine Abnormalities Associated With TUBB3 E410K Syndrome

CONTEXT: A heterozygous de novo c.1228G>A mutation (E410K) in the TUBB3 gene encoding the neuronal-specific β-tubulin isotype 3 (TUBB3) causes the TUBB3 E410K syndrome characterized by congenital fibrosis of the extraocular muscles (CFEOM), facial weakness, intellectual and social disabilities, a...

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Опубликовано в: :J Clin Endocrinol Metab
Главные авторы: Balasubramanian, Ravikumar, Chew, Sheena, MacKinnon, Sarah E., Kang, Peter B., Andrews, Caroline, Chan, Wai-Man, Engle, Elizabeth C.
Формат: Artigo
Язык:Inglês
Опубликовано: Endocrine Society 2015
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Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC4333039/
https://ncbi.nlm.nih.gov/pubmed/25559402
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1210/jc.2014-4107
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