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Severity score for hereditary hemorrhagic telangiectasia
BACKGROUND: A disease severity score in hereditary hemorrhagic telangiectasia (HHT) would be a useful tool for assessing burden of disease and for designing clinical trials. Here, we propose the first known HHT severity score, the HHT-score. METHODS: Demographics and disease characteristics were col...
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| Опубликовано в: : | Orphanet J Rare Dis |
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| Главные авторы: | , , , , , |
| Формат: | Artigo |
| Язык: | Inglês |
| Опубликовано: |
BioMed Central
2014
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| Предметы: | |
| Online-ссылка: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4302697/ https://ncbi.nlm.nih.gov/pubmed/25928712 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-014-0188-3 |
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