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A comparison of interventional clinical trials in rare versus non-rare diseases: an analysis of ClinicalTrials.gov

OBJECTIVES: To provide a comprehensive characterisation of rare disease clinical trials registered in ClinicalTrials.gov, and compare against characteristics of trials in non-rare diseases. DESIGN: Registry based study of ClinicalTrials.gov registration entries. METHODS: The ClinicalTrials.gov regis...

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Pubblicato in:Orphanet J Rare Dis
Autori principali: Bell, Stuart A, Tudur Smith, Catrin
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2014
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4255432/
https://ncbi.nlm.nih.gov/pubmed/25427578
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-014-0170-0
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