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Carnitine Profile and Effect of Suppletion in Children with Renal Fanconi Syndrome due to Cystinosis

Background: Cystinosis is an autosomal recessive disorder marked by intralysosomal cystine accumulation. Patients present with generalized proximal tubular dysfunction called renal Fanconi syndrome. Urinary carnitine loss results in plasma and muscle carnitine deficiency, but no clinical signs of ca...

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Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:JIMD Rep
Egile Nagusiak: Besouw, M., Cornelissen, E., Cassiman, D., Kluijtmans, L., van den Heuvel, L., Levtchenko, E.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Springer Berlin Heidelberg 2014
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC4221611/
https://ncbi.nlm.nih.gov/pubmed/24798266
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2014_312
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