Enzyme Replacement Therapy in Mucopolysaccharidosis II Patients Under 1 Year of Age

Mucopolysaccharidosis (MPS) II, or Hunter syndrome, is a lysosomal storage disease characterized by multi-systemic involvement and a progressive clinical course. Enzyme replacement therapy with idursulfase has been approved in more than 50 countries worldwide; however, safety and efficacy data from...

Descrición completa

Gardado en:
Detalles Bibliográficos
Main Authors: Lampe, Christina, Atherton, Andrea, Burton, Barbara K., Descartes, Maria, Giugliani, Roberto, Horovitz, Dafne D. G., Kyosen, Sandra O., Magalhães, Tatiana S. P. C., Martins, Ana Maria, Mendelsohn, Nancy J., Muenzer, Joseph, Smith, Laurie D.
Formato: Artigo
Idioma:Inglês
Publicado: Springer Berlin Heidelberg 2014
Assuntos:
Article
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC4213327/
https://ncbi.nlm.nih.gov/pubmed/24515576
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2013_289
Tags: Engadir etiqueta
Sen Etiquetas, Sexa o primeiro en etiquetar este rexistro!

Títulos similares