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A symptomatic Fabry disease mouse model generated by inducing globotriaosylceramide synthesis

Fabry disease is a lysosomal storage disorder in which neutral glycosphingolipids, predominantly globotriaosylceramide (Gb3), accumulate due to deficient α-galactosidase A (α-Gal A) activity. The α-Gal A-knockout (GLAko) mouse has been used as a model for Fabry disease, but it does not have any symp...

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Detalhes bibliográficos
Main Authors: Taguchi, Atsumi, Maruyama, Hiroki, Nameta, Masaaki, Yamamoto, Tadashi, Matsuda, Junichiro, Kulkarni, Ashok B., Yoshioka, Hidekatsu, Ishii, Satoshi
Formato: Artigo
Idioma:Inglês
Publicado em: 2013
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4160053/
https://ncbi.nlm.nih.gov/pubmed/24094090
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1042/BJ20130825
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