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RNAi-based Gene Therapy for Dominant Limb Girdle Muscular Dystrophies

Limb Girdle Muscular Dystrophy (LGMD) refers to a group of 25 genetic diseases linked by common clinical features, including wasting of muscles supporting the pelvic and shoulder girdles. Cardiac involvement may also occur. Like other muscular dystrophies, LGMDs are currently incurable, but prospect...

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Detalhes bibliográficos
Main Authors: Liu, Jian, Harper, Scott Q.
Formato: Artigo
Idioma:Inglês
Publicado em: 2012
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4120526/
https://ncbi.nlm.nih.gov/pubmed/22856606
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