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RNAi-based Gene Therapy for Dominant Limb Girdle Muscular Dystrophies

Limb Girdle Muscular Dystrophy (LGMD) refers to a group of 25 genetic diseases linked by common clinical features, including wasting of muscles supporting the pelvic and shoulder girdles. Cardiac involvement may also occur. Like other muscular dystrophies, LGMDs are currently incurable, but prospect...

Täydet tiedot

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Bibliografiset tiedot
Päätekijät: Liu, Jian, Harper, Scott Q.
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: 2012
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC4120526/
https://ncbi.nlm.nih.gov/pubmed/22856606
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