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In vivo activation of the human δ-globin gene: the therapeutic potential in β-thalassemic mice

β-thalassemia and sickle cell disease are widespread fatal genetic diseases. None of the existing clinical treatments provides a solution for all patients. Two main strategies for treatment are currently being investigated: (i) gene transfer of a normal β-globin gene; (ii) reactivation of the endoge...

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Detalhes bibliográficos
Main Authors: Manchinu, Maria F., Marongiu, Maria F., Poddie, Daniela, Casu, Carla, Latini, Veronica, Simbula, Michela, Galanello, Renzo, Moi, Paolo, Cao, Antonio, Porcu, Susanna, Ristaldi, Maria S.
Formato: Artigo
Idioma:Inglês
Publicado em: Ferrata Storti Foundation 2014
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4007936/
https://ncbi.nlm.nih.gov/pubmed/23872310
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3324/haematol.2012.082768
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