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Congenital disorders of glycosylation with neonatal presentation

Congenital disorders of glycosylation (CDG) are a group of hereditary diseases characterised by deficiency of enzymes involved in proteins glycosylation. We describe the clinical case of a neonate with CDG type 1a, nowadays designated phosphomannomutase 2 (PMM2)-CDG. Physical examination showed an a...

Täydet tiedot

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Bibliografiset tiedot
Päätekijät: Resende, Catarina, Carvalho, Carmen, Alegria, Artur, Oliveira, Dulce, Quelhas, Dulce, Bandeira, Anabela, Proença, Elisa
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: BMJ Publishing Group 2014
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC3992553/
https://ncbi.nlm.nih.gov/pubmed/24739649
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/bcr-2013-010037
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