Long-term in vitro correction of alpha-L-iduronidase deficiency (Hurler syndrome) in human bone marrow.

Allogeneic bone marrow transplantation is the most effective treatment for Hurler syndrome but, since this therapy is not available to all patients, we have considered an alternative approach based on transfer and expression of the normal gene in autologous bone marrow. A retroviral vector carrying...

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Detaylı Bibliyografya
Asıl Yazarlar: Fairbairn, L J, Lashford, L S, Spooncer, E, McDermott, R H, Lebens, G, Arrand, J E, Arrand, J R, Bellantuono, I, Holt, R, Hatton, C E, Cooper, A, Besley, G T, Wraith, J E, Anson, D S, Hopwood, J J, Dexter, T M
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: 1996
Konular:
Research Article
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC39903/
https://ncbi.nlm.nih.gov/pubmed/8700879
Etiketler: Etiketle
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