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Restoration of cone vision in a mouse model of achromatopsia

Loss of cone function in the central retina is a pivotal event in the development of severe vision impairment for many prevalent blinding diseases. Complete achromatopsia is a genetic defect resulting in cone vision loss in 1 in 30,000 individuals. Using adeno-associated virus (AAV) gene therapy, we...

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Detalhes bibliográficos
Main Authors: Alexander, John J, Umino, Yumiko, Everhart, Drew, Chang, Bo, Min, Seok H, Li, Qiuhong, Timmers, Adrian M, Hawes, Norman L, Pang, Ji-jing, Barlow, Robert B, Hauswirth, William W
Formato: Artigo
Idioma:Inglês
Publicado em: 2007
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC3985124/
https://ncbi.nlm.nih.gov/pubmed/17515894
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/nm1596
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