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Prednisolone improves walking in Japanese Duchenne muscular dystrophy patients

We evaluated the long-term efficacy of prednisolone (PSL) therapy for prolonging ambulation in Japanese patients with genetically confirmed Duchenne muscular dystrophy (DMD). There were clinical trials have shown a short-term positive effect of high-dose and daily PSL on ambulation, whereas a few st...

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Autores principales: Takeuchi, Fumi, Yonemoto, Naohiro, Nakamura, Harumasa, Shimizu, Reiko, Komaki, Hirofumi, Mori-Yoshimura, Madoka, Hayashi, Yukiko K., Nishino, Ichizo, Kawai, Mitsuru, Kimura, En, Takeda, Shin’ichi
Formato: Artigo
Lenguaje:Inglês
Publicado: Springer Berlin Heidelberg 2013
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC3843366/
https://ncbi.nlm.nih.gov/pubmed/24057148
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s00415-013-7104-y
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