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In vitro antisense therapeutics for a deep intronic mutation causing Neurofibromatosis type 2

Neurofibromatosis type 2 (NF2) is an autosomal-dominant disorder affecting about 1:33 000 newborns, mainly characterized by the development of tumors of the nervous system and ocular abnormalities. Around 85% of germline NF2 mutations are point mutations. Among them, ∼25% affect splicing and are ass...

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Detalhes bibliográficos
Main Authors: Castellanos, Elisabeth, Rosas, Imma, Solanes, Ares, Bielsa, Isabel, Lázaro, Conxi, Carrato, Cristina, Hostalot, Cristina, Prades, Pepe, Roca-Ribas, Francesc, Blanco, Ignacio, Serra, Eduard
Formato: Artigo
Idioma:Inglês
Publicado em: Nature Publishing Group 2013
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC3722955/
https://ncbi.nlm.nih.gov/pubmed/23188051
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/ejhg.2012.261
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