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Relationship Between Clinical Outcome Measures and Parent Proxy Reports of Health-related Quality of Life in Ambulatory Children with Duchenne Muscular Dystrophy

In Duchenne muscular dystrophy, data directly linking changes in clinical outcome measures to patient-perceived well-being are lacking. Our study evaluated the relationship between clinical outcome measures used in clinical trials of ambulatory Duchenne muscular dystrophy (Vignos functional grade, q...

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Bibliografiske detaljer
Main Authors: McDonald, Craig M., McDonald, Dawn A., Bagley, Anita M., Sienko-Thomas, Susan, Buckon, Cathleen, Henricson, Eric, Nicorici, Alina, Sussman, Michael D.
Format: Artigo
Sprog:Inglês
Udgivet: 2010
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC3695468/
https://ncbi.nlm.nih.gov/pubmed/20558672
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1177/0883073810371509
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