Wird geladen...

Antibody formation and mannose-6-phosphate receptor expression impact the efficacy of muscle-specific transgene expression in murine Pompe disease

BACKGROUND: Lysosomal storage disorders such as Pompe disease can be more effectively treated, if immune tolerance to enzyme or gene replacement therapy can be achieved. Alternatively, immune responses against acid α-glucosidase (GAA) might be evaded in Pompe disease through muscle-specific expressi...

Ausführliche Beschreibung

Gespeichert in:
Bibliographische Detailangaben
Hauptverfasser: Sun, Baodong, Li, Songtao, Bird, Andrew, Yi, Haiqing, Kemper, Alex, Koeberl, Dwight D.
Format: Artigo
Sprache:Inglês
Veröffentlicht: 2010
Schlagworte:
Online Zugang:https://ncbi.nlm.nih.gov/pmc/articles/PMC3655728/
https://ncbi.nlm.nih.gov/pubmed/20967919
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jgm.1511
Tags: Tag hinzufügen
Keine Tags, Fügen Sie den ersten Tag hinzu!