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Antisense Oligonucleotides: Rising Stars in Eliminating RNA Toxicity in Myotonic Dystrophy

Myotonic dystrophy (DM) is a dominantly inherited, multisystemic disease caused by expanded CTG (type 1, DM1) or CCTG (type 2, DM2) repeats in untranslated regions of the mutated genes. Pathogenesis results from expression of RNAs from the mutated alleles that are toxic because of the expanded CUG o...

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Bibliographic Details
Main Authors: Gao, Zhihua, Cooper, Thomas A.
Format: Artigo
Language:Inglês
Published: Mary Ann Liebert, Inc. 2013
Subjects:
Online Access:https://ncbi.nlm.nih.gov/pmc/articles/PMC3655630/
https://ncbi.nlm.nih.gov/pubmed/23252746
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2012.212
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