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GM1gangliosidosis: Clinical and radiological clue to diagnosis

GM1gangliosidosis is a rare autosomal recessive lysosomal storage disorder caused by deficiency of enzyme β-galactosidase, resulting in progressive neural and visceral accumulation of GM1gangliosides. Coarse facial features, bilateral cherry red spots, and dysostosis multiplex are important clue to...

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Bibliografiske detaljer
Main Authors: Suthar, Renu, Sahu, Jitendra K., Singhi, Pratibha
Format: Artigo
Sprog:Inglês
Udgivet: Medknow Publications & Media Pvt Ltd 2012
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC3611903/
https://ncbi.nlm.nih.gov/pubmed/23560001
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4103/1817-1745.106472
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